Sarepta is facing a number of issues currently, including platform-level safety concerns, management credibility issues, etc.

The approval makes donidalorsen the only treatment in the US for hereditary angioedema that is an RNA-targeted prophylactic.

As aging progresses, the quality of DNA and proteins inside cells declines, which is known to be the cause of various ...

Researchers at San Diego State University and Michigan State University are shedding new light on how viruses meticulously ...

In 1957, just four years after Francis Crick and other scientists solved the riddle of DNA’s structure—the now famous double ...

Similar to the way the caps on the ends of a shoelace prevent it from fraying, telomeres—regions of repetitive DNA sequences ...

Genomics, Inc. (Nasdaq: TXG), a leader in single cell and spatial biology, today announced the launch of Xenium Protein, a ...

Using artificial intelligence, MIT researchers have come up with a new way to design nanoparticles that can more efficiently ...

Since 2008, the FDA has approved 11 treatments for a rare genetic condition called hereditary angioedema (HAE), three of ...

Rapid precision run-on sequencing (rPRO-seq) may help doctors understand disease states and treatment response in real time.

Researchers at Sylvester Comprehensive Cancer Center, part of the University of Miami Miller School of Medicine, have ...

A previously unknown virus in farmed Pacific oysters may hold the key to mass die-offs in the multimillion-dollar industry, according to research from the University of British Columbia (UBC) in ...